ATMP Horizon

Nordic HTA case detection
⬇ CSV

50 tracked ATMP cases. gold = no Danish (Medicinrådet) decision yet

✓ 6 sources checked, all parsed · last 18 Aug 2026.

Nordic decisions

33
ProductIndication SverigeNorgeDanmark
Abecma MM Avbestilt
Alofisel Crohn perianal fistula Innføres Ikke anbefalet
Aucatzyl ALL avvakta
Breyanzi DLBCL Innføres
Breyanzi MCL kan användas
Breyanzi DLBCL 3L kan användas Anbefalet
Breyanzi DLBCL 2L Anbefalet
Carvykti MM 2L kan användas
Carvykti MM Innføres ikke Anbefalet
Casgevy SCD avvakta Anbefalet
Casgevy TDT Anbefalet
Ebvallo EBV+ PTLD bör användas Innføres
Hemgenix Hemophilia använd inte Innføres
Holoclar Limbal stem cell deficiency Delvist anbefalet
Imlygic Melanoma Innføres ikke
Kymriah DLBCL Innføres ikke
Kymriah FL använd inte Avbestilt
Kymriah DLBCL 3L använd inte
Kymriah ALL kan användas Innføres Anbefalet
lenadogene nolparvovec LHON Avbestilt
Libmeldy MLD bör användas Innføres
Luxturna RPE65 retinal dystrophy bör användas Videreføres Anbefalet
Roctavian Hemophilia Ikke lansert i Norge
Tecartus ALL kan användas Innføres
Tecartus MCL kan användas Innføres Ikke anbefalet
Upstaza AADC deficiency bör användas Innføres ikke
Vyjuvek DEB avvakta
Yescarta DLBCL Innføres
Yescarta FL avvakta Innføres ikke
Yescarta DLBCL 3L kan användas
Yescarta DLBCL 2L kan användas Anbefalet
Zolgensma SMA bör användas Under revurdering Anbefalet
Zynteglo TDT Innføres ikke

Horizon

5

Upstream EU pipeline (PRIME / JCA / CHMP) — detected early, not yet authorised.

ProductIndicationATMPLatest signalStage
bilayer engineered skin composed of autologous keratinocytes and allogeneic fibroblasts embedded in an allogeneic plasma matrix Treatment of adults and children with partial deep... CONFIRMED EMA-CHMP · under evaluation
2026-08-18
3
lunsotogene parvec Treatment of biallelic OTOF variant-associated hearing... CONFIRMED EMA-CHMP · under evaluation
2026-08-18
3
zamtocabtagene autoleucel Treatment of adults with large B-cell lymphoma CONFIRMED EMA-CHMP · under evaluation · PRIME
2026-08-18
3
zopapogene imadenovec Treatment of respiratory papillomatosis in adults CONFIRMED EMA-CHMP · under evaluation
2026-08-18
3
autologous melanoma-derived tumor infiltrating lymphocytes, ex vivo-expanded No longer listed Treatment of melanoma CONFIRMED EMA-CHMP · no longer listed
2026-08-05
3

Authorised — pending national assessment

12

EU-authorised ATMPs with no Nordic verdict yet — sorted by time waiting (longest first).

ProductIndicationATMPLatest signalStage Since EU auth
ChondroCelect Withdrawn
TiGenix N.V.
Cartilage Diseases CONFIRMED EMA · withdrawn
2026-08-18
4 16.9 yr
Glybera Expired
uniQure biopharma B.V.
Hyperlipoproteinemia Type I CONFIRMED EMA · expired
2026-08-18
4 13.8 yr
Maci Expired
Vericel Denmark ApS
Fractures, Cartilage CONFIRMED EMA · expired
2026-08-18
4 13.2 yr
Provenge Withdrawn
Dendreon UK Ltd
Prostatic Neoplasms CONFIRMED EMA · withdrawn
2026-08-18
4 13.0 yr
Strimvelis
Fondazione Telethon ETS
Severe Combined Immunodeficiency CONFIRMED EMA · authorised
2026-08-18
4 10.3 yr
no DK decision
Zalmoxis Withdrawn
MolMed SpA
Hematopoietic Stem Cell Transplantation;Graft vs Host Disease CONFIRMED EMA · withdrawn
2026-08-18
4 10.0 yr
Spherox
CO.DON Gmbh
Cartilage Diseases CONFIRMED EMA · authorised
2026-08-18
4 9.1 yr
no DK decision
Skysona Withdrawn
bluebird bio (Netherlands) B.V.
Adrenoleukodystrophy CONFIRMED EMA · withdrawn
2026-08-18
4 5.1 yr
Beqvez (previously Durveqtix) Withdrawn
Pfizer Europe MA EEIG
Hemophilia B CONFIRMED EMA · withdrawn
2026-08-18
4 2.1 yr
Zemcelpro
Cordex Biologics International Limited
Hematologic Neoplasms;Hematopoietic Stem Cell Transplantation CONFIRMED EMA · authorised
2026-08-18
4 1.0 yr
no DK decision
Waskyra
Fondazione Telethon ETS
Wiskott-Aldrich Syndrome CONFIRMED EMA · authorised
2026-08-18
4 0.6 yr
no DK decision
Adstiladrin
Ferring Pharmaceuticals A/S
Non-Muscle Invasive Bladder Neoplasms CONFIRMED EMA · authorised
2026-08-18
4 0.2 yr
no DK decision