ATMP Horizon

Nordic HTA case detection

← Board

Waskyra CONFIRMED

etuvetidigene autotemcel · Wiskott-Aldrich Syndrome

Current stage: 4 · first detected 2026-06-25

Also known as: waskyra

CompanyFondazione Telethon ETS
ATC codeB06
EU authorised2026-01-09 · 0 yr ago
Flags Orphan
EMA EPAR Evidence dossier ↗

Status timeline

DateBodyStatusStageSource
2026-06-25 EMA authorised 4 link