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Nordic HTA case detection

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Upstaza CONFIRMED

eladocagene exuparvovec · AADC deficiency

Current stage: 6 · first detected 2026-06-25

Also known as: upstaza

CompanyPTC Therapeutics International Limited
ATC codeA16AB26
EU authorised2022-07-18 · 3 yr ago
Flags Orphan
EMA EPAR Evidence dossier ↗

Nordic decisions

CountryBodyVerdictDateSource
Sverige NT-rådet bör användas 2026-06-12 link
Norge Beslutningsforum Innføres ikke 2025-04-28 link

Status timeline

DateBodyStatusStageSource
No status history.