ATMP Horizon

Nordic HTA case detection

rebisufligene etisparvovec CONFIRMED

rebisufligene etisparvovec · Treatment of Mucopolysaccharidosis Type IIIA, MPS IIIA (Sanfilippo A Syndrome) in children from birth to 18 years old

Current stage: 3 · first detected 2026-10-13

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Date	Body	Status	Stage	Source
2026-10-13	EMA-CHMP	under evaluation	3	link